Drépanocytose et thalassémie : un traitement révolutionnaire vient d’être autorisé!
L’Agence de réglementation des médicaments et des produits de santé (MHRA) au Royaume-Uni, vient d’approuver un traitement révolutionnaire contre la drépanocytose et la β-thalassémie : Casgevy.
Ce médicament innovant, le premier à utiliser la technologie CRISPR, récompensé par un prix Nobel en 2020, ouvre une nouvelle ère dans le traitement de ces maladies génétiques. Avec des résultats prometteurs dans les essais cliniques et une approche unique de modification génétique, Casgevy représente un espoir considérable pour améliorer la qualité de vie des patients.
La drépanocytose et la β-thalassémie sont causées par des erreurs génétiques dans la production de l’hémoglobine. Ces maladies sont particulièrement répandues chez les individus d’origine africaine, caribéenne, méditerranéenne, sud-asiatique, sud-est asiatique et moyen-orientale. La drépanocytose se manifeste par des crises de douleur intense, des infections graves et une anémie, tandis que la β-thalassémie entraîne une anémie sévère nécessitant des transfusions régulières.
Casgevy agit en modifiant le gène défectueux dans les cellules souches de la moelle osseuse du patient. Celles-ci sont prélevées, génétiquement modifiées, puis réinjectées au patient. Jusqu’à présent, la greffe de moelle osseuse était la seule solution pour ces patients, malgré son risque de rejet. Durant les essais, Casgevy a démontré sa capacité à restaurer la production d’hémoglobine normale et saine.
Dans l’essai pour la drépanocytose, 97 % des patients traités n’ont pas eu de crise de douleur sévère pendant au moins 12 mois. Pour la β-thalassémie, 93 % des patients n’ont pas eu besoin de transfusion sanguine pendant au moins un an après le traitement. Les effets secondaires étaient similaires à ceux des greffes de cellules souches autologues, incluant nausée et fatigue.
Source: Futurascience
Awsome post and straight to the point. I am not sure
if this is really the best place to ask but do you people have any thoughts on where to hire some professional writers?
Thank you 🙂 Lista escape room
Very interesting information!Perfect just what I was looking for!?
You have observed very interesting details! ps nice web site.
Travel guide
Your point of view caught my eye and was very interesting. Thanks. I have a question for you.
Thank you for your sharing. I am worried that I lack creative ideas. It is your article that makes me full of hope. Thank you. But, I have a question, can you help me?
This page definitely has all of the information and facts I wanted about this subject and didn’t know who to ask.
Aw, this was a really nice post. Spending some time and actual effort to generate a very good article… but what can I say… I put things off a lot and never manage to get anything done.
This website truly has all of the information I needed about this subject and didn’t know who to ask.
I blog often and I genuinely appreciate your content. Your article has really peaked my interest. I am going to book mark your blog and keep checking for new information about once per week. I subscribed to your RSS feed too.
Great article! We will be linking to this great post on our website. Keep up the good writing.
Aw, this was a very good post. Taking the time and actual effort to make a great article… but what can I say… I hesitate a whole lot and don’t seem to get anything done.
Hi! I just would like to give you a huge thumbs up for your great info you have got right here on this post. I will be coming back to your blog for more soon.
This site definitely has all the information and facts I wanted concerning this subject and didn’t know who to ask.
Thanks for sharing. I read many of your blog posts, cool, your blog is very good.
I love it when folks come together and share ideas. Great blog, continue the good work!
This page really has all the information and facts I needed concerning this subject and didn’t know who to ask.
I truly love your website.. Pleasant colors & theme. Did you make this website yourself? Please reply back as I’m attempting to create my own personal website and would love to learn where you got this from or exactly what the theme is called. Cheers.
I could not refrain from commenting. Perfectly written.
I blog frequently and I truly appreciate your information. This great article has really peaked my interest. I’m going to book mark your site and keep checking for new details about once a week. I opted in for your RSS feed too.
Can I simply just say what a relief to discover somebody that really understands what they’re discussing on the net. You actually understand how to bring an issue to light and make it important. A lot more people really need to look at this and understand this side of your story. I was surprised that you are not more popular because you definitely have the gift.
Thanks for sharing. I read many of your blog posts, cool, your blog is very good.
Aw, this was a very good post. Taking a few minutes and actual effort to generate a great article… but what can I say… I put things off a lot and never manage to get anything done.
Hi there! I could have sworn I’ve been to this site before but after browsing through a few of the articles I realized it’s new to me. Nonetheless, I’m certainly happy I discovered it and I’ll be book-marking it and checking back regularly.
I don’t think the title of your article matches the content lol. Just kidding, mainly because I had some doubts after reading the article.
Your article helped me a lot, is there any more related content? Thanks!
Nice post. I learn something new and challenging on websites I stumbleupon every day. It’s always helpful to read content from other authors and practice something from their websites.
Your style is really unique in comparison to other folks I’ve read stuff from. Many thanks for posting when you’ve got the opportunity, Guess I’ll just bookmark this page.
An outstanding share! I’ve just forwarded this onto a coworker who has been doing a little homework on this. And he in fact bought me breakfast due to the fact that I stumbled upon it for him… lol. So let me reword this…. Thanks for the meal!! But yeah, thanks for spending the time to discuss this subject here on your website.
After I initially commented I seem to have clicked on the -Notify me when new comments are added- checkbox and now each time a comment is added I get four emails with the exact same comment. Perhaps there is a means you can remove me from that service? Many thanks.
Everything is very open with a clear explanation of the challenges. It was truly informative. Your site is useful. Thank you for sharing.
bookmarked!!, I really like your site.
I used to be able to find good info from your blog posts.
You ought to be a part of a contest for one of the greatest sites on the net. I most certainly will highly recommend this site!
Can you be more specific about the content of your article? After reading it, I still have some doubts. Hope you can help me.
For several years, I’ve battled unforeseeable blood sugar swings that left me feeling drained pipes
and tired. But given that integrating Sugar Protector
right into my routine, I have actually noticed a considerable renovation in my total power and stability.
The dreaded mid-day distant memory, and I value that
this all-natural solution achieves these outcomes with no unpleasant or adverse responses.
honestly been a transformative exploration for me.
Adding Sugar Defender to my daily regimen was one of the most
effective decisions I’ve produced my health.
I’m careful concerning what I consume, however this supplement
includes an added layer of support. I feel extra stable throughout
the day, and my food cravings have reduced dramatically.
It’s nice to have something so basic that makes such a huge distinction!
Your point of view caught my eye and was very interesting. Thanks. I have a question for you.
I have to thank you for the efforts you’ve put in penning this site. I really hope to check out the same high-grade blog posts by you later on as well. In fact, your creative writing abilities has encouraged me to get my very own blog now 😉
An impressive share! I have just forwarded this onto a co-worker who has been doing a little homework on this. And he actually ordered me lunch because I stumbled upon it for him… lol. So let me reword this…. Thanks for the meal!! But yeah, thanx for spending time to talk about this subject here on your internet site.
Spot on with this write-up, I truly believe this web site needs a great deal more attention. I’ll probably be back again to read more, thanks for the information!
Good day! Do you know if they make any plugins to
assist with SEO? I’m trying to get my website to rank for some targeted keywords but I’m
not seeing very good gains. If you know of any please share.
Thank you! You can read similar text here: Warm blankets
Thanks for sharing. I read many of your blog posts, cool, your blog is very good.
This is a topic that’s close to my heart… Take care! Where are your contact details though?
I love reading a post that can make men and women think. Also, thank you for allowing me to comment.
Aw, this was an incredibly nice post. Finding the time and actual effort to produce a very good article… but what can I say… I procrastinate a whole lot and never seem to get nearly anything done.
I must thank you for the efforts you’ve put in writing this blog. I am hoping to view the same high-grade content by you later on as well. In truth, your creative writing abilities has encouraged me to get my own blog now 😉
Good article! We will be linking to this particularly great content on our website. Keep up the great writing.
Great web site you have here.. It’s difficult to find excellent writing like yours these days. I seriously appreciate individuals like you! Take care!!
Oh my goodness! Amazing article dude! Thanks, However I am experiencing problems with your RSS. I don’t understand the reason why I am unable to subscribe to it. Is there anybody getting the same RSS issues? Anyone who knows the solution will you kindly respond? Thanks!!
There is no motive why a camping trip ought to go improper.
There is certainly a great deal to learn about this subject. I really like all the points you have made.
Can you be more specific about the content of your article? After reading it, I still have some doubts. Hope you can help me.
This page certainly has all of the information and facts I needed about this subject and didn’t know who to ask.
Your point of view caught my eye and was very interesting. Thanks. I have a question for you.
Excellent post! We are linking to this great content on our website. Keep up the good writing.
I’m extremely pleased to find this page. I wanted to thank you for your time for this wonderful read!! I definitely liked every little bit of it and i also have you saved as a favorite to check out new information in your website.
I used to be able to find good information from your blog articles.
Thanks for sharing. I read many of your blog posts, cool, your blog is very good.
Greetings! Very helpful advice within this post! It’s the little changes that make the greatest changes. Many thanks for sharing!
I seriously love your website.. Excellent colors & theme. Did you create this amazing site yourself? Please reply back as I’m wanting to create my own personal website and would like to learn where you got this from or exactly what the theme is named. Thank you!
Your style is very unique compared to other people I have read stuff from. I appreciate you for posting when you have the opportunity, Guess I will just bookmark this page.
This is a topic that is near to my heart… Cheers! Exactly where can I find the contact details for questions?
Great post. I am dealing with a few of these issues as well..
An outstanding share! I’ve just forwarded this onto a coworker who has been doing a little research on this. And he actually bought me breakfast because I discovered it for him… lol. So let me reword this…. Thanks for the meal!! But yeah, thanks for spending some time to discuss this matter here on your web site.
I’m impressed, I have to admit. Seldom do I encounter a blog that’s both educative and engaging, and let me tell you, you have hit the nail on the head. The issue is something that not enough men and women are speaking intelligently about. Now i’m very happy I found this during my hunt for something concerning this.
<a href="https://r.ypcdn.com/1/c/rtd?ptid=YWSIR
Spot on with this write-up, I seriously believe that this web site needs much more attention. I’ll probably be back again to read more, thanks for the information.
I was able to find good advice from your content.
<a href="https://auth.she.com/logout/?callback=https://thailandgameshow.weebly.com/
This is a good tip especially to those new to the blogosphere. Short but very precise info… Many thanks for sharing this one. A must read post!
I couldn’t resist commenting. Well written.
An outstanding share! I’ve just forwarded this onto a colleague who was conducting a little homework on this. And he in fact bought me lunch because I stumbled upon it for him… lol. So allow me to reword this…. Thanks for the meal!! But yeah, thanks for spending time to discuss this matter here on your blog.
I enjoy reading a post that will make people think. Also, many thanks for permitting me to comment.
Thank you for your sharing. I am worried that I lack creative ideas. It is your article that makes me full of hope. Thank you. But, I have a question, can you help me?
Your style is so unique compared to other folks I have read stuff from. I appreciate you for posting when you have the opportunity, Guess I’ll just bookmark this web site.
I needed to thank you for this fantastic read!! I absolutely enjoyed every bit of it. I’ve got you saved as a favorite to look at new things you post…
After looking at a number of the blog posts on your website, I honestly like your way of writing a blog. I book-marked it to my bookmark webpage list and will be checking back soon. Take a look at my web site too and let me know what you think.
Very good information. Lucky me I found your blog by chance (stumbleupon). I have saved as a favorite for later!
gamepg.weebly.com
Howdy, I do think your web site may be having browser compatibility issues. Whenever I look at your blog in Safari, it looks fine however, when opening in Internet Explorer, it’s got some overlapping issues. I simply wanted to provide you with a quick heads up! Other than that, fantastic blog.
Hello! I simply would like to offer you a big thumbs up for your excellent information you have right here on this post. I will be coming back to your site for more soon.
Pretty! This has been a really wonderful post. Thank you for supplying this information.
If the room already features a vivid, bold colour at the partitions, a extra delicate palette may be most well-liked for the window remedy.
You’re so cool! I do not think I’ve truly read through anything like this before. So great to discover someone with unique thoughts on this topic. Seriously.. thanks for starting this up. This website is one thing that is needed on the internet, someone with a little originality.
Hello there! This article couldn’t be written much better! Going through this post reminds me of my previous roommate! He continually kept preaching about this. I will send this article to him. Pretty sure he’ll have a very good read. Thanks for sharing!
After exploring a number of the articles on your site, I really appreciate your way of writing a blog. I added it to my bookmark website list and will be checking back soon. Take a look at my website as well and let me know what you think.
Good post. I learn something new and challenging on sites I stumbleupon every day. It’s always helpful to read through articles from other authors and practice a little something from their web sites.
This is the perfect website for anybody who wishes to find out about this topic. You realize a whole lot its almost tough to argue with you (not that I really will need to…HaHa). You certainly put a fresh spin on a topic which has been written about for a long time. Wonderful stuff, just excellent.
I don’t think the title of your article matches the content lol. Just kidding, mainly because I had some doubts after reading the article.
It’s hard to come by experienced people about this topic, however, you seem like you know what you’re talking about! Thanks
This is a topic that is near to my heart… Take care! Where can I find the contact details for questions?
People in every single place in India are really feel safe searching for the newest Indian online jewellery without any menace to their financial info in any respect.
Everything is very open with a clear description of the issues. It was really informative. Your website is extremely helpful. Thanks for sharing!
Aw, this was a really good post. Taking the time and actual effort to create a superb article… but what can I say… I put things off a lot and don’t manage to get nearly anything done.
I really like it when folks come together and share views. Great blog, keep it up!
I’m impressed, I must say. Seldom do I come across a blog that’s equally educative and entertaining, and let me tell you, you have hit the nail on the head. The problem is something which too few men and women are speaking intelligently about. I’m very happy I came across this during my hunt for something relating to this.
This page really has all of the information and facts I needed concerning this subject and didn’t know who to ask.
Your article helped me a lot, is there any more related content? Thanks!
Excellent site you have got here.. It’s difficult to find good quality writing like yours these days. I seriously appreciate people like you! Take care!!
Very nice post. I absolutely love this site. Continue the good work!
I’d like to thank you for the efforts you have put in penning this website. I really hope to view the same high-grade blog posts by you later on as well. In fact, your creative writing abilities has motivated me to get my own site now 😉
I love it whenever people come together and share thoughts. Great website, stick with it!
After exploring a number of the blog posts on your website, I seriously like your technique of writing a blog. I added it to my bookmark webpage list and will be checking back soon. Please visit my web site too and tell me what you think.
I enjoy reading through a post that will make men and women think. Also, many thanks for allowing for me to comment.
Spot on with this write-up, I honestly believe that this web site needs a lot more attention. I’ll probably be back again to see more, thanks for the advice!
Greetings! Very helpful advice in this particular post! It is the little changes that produce the most significant changes. Thanks a lot for sharing!
I really like it when individuals get together and share thoughts. Great website, keep it up!
Thanks for sharing. I read many of your blog posts, cool, your blog is very good.
A muscular Russian lady, Steve Hong’s bodyguard, who trains Daniel to reduce his weight.
Although most people who are infected with West Nile virus never get sick, the virus may cause meningitis (a swelling of the membrane around the brain and spinal cord) and encephalitis.